Combined assessment of early and late-phase outcomes in orphan drug development (Q6627849)
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scientific article; zbMATH DE number 7934435
| Language | Label | Description | Also known as |
|---|---|---|---|
| English | Combined assessment of early and late-phase outcomes in orphan drug development |
scientific article; zbMATH DE number 7934435 |
Statements
Combined assessment of early and late-phase outcomes in orphan drug development (English)
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29 October 2024
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Bayesian
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bias correction
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biomarker
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borrowing strength
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decision-induced bias
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rare diseases
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surrogate endpoint
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trial combination
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